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FrancoAngeli Journals

Saggi

No. 128 (2023)

Managing the complexity of change: Introducing a therapeutic innovation for SMA in two Italian Regions

DOI
https://doi.org/10.3280/mesa2023-128oa18586
Submitted
ottobre 1, 2024
Published
2024-11-28

Abstract

The paper presents the implementation of the therapeutic management path of patients being treated with a drug for Spinal Muscular Atrophy (SMA) in two regional Italian contexts, focusing on the role of multi-professional networks.
Through interviews with professionals involved in therapeutic management at the “Città della Salute e della Scienza” University Hospital in Turin, the “Città di Torino”
Local Health Authority, and the Marche Region Health Service (ASUR), the work highlights the complexity of introducing therapeutic innovations for rare diseases. The context, pharmaceutical management policies, drug access, and challenges in providing care for SMA patients are examined in detail. It describes how multi-professional involvement and organization among hospital centers have facilitated the access to treatment while identifying future training challenges and new medication management.

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